Total number of Results for PiZ hepatocytes are 1
ASPsiDb_ID Mutant allele/ASP-siRNA Mutant
efficacy (%)
Wild
efficacy (%)
Percentage
discrimination (%)
Gene Disease Analysis Pubmed ID
ASPsiDb_ID Mutant allele/ASP-siRNA Mutant
efficacy (%)
Wild
efficacy (%)
Percentage
discrimination (%)
Gene Disease Analysis Pubmed ID
aspsirna1947 GACCCCAGGCTCCACCAAA
CUGGGGUCCGTGGUGGUUU
80 14 66 SERPINA1/Alpha-1 antitrypsin (AAT) Emphysema/Alpha-1 antitrypsin deficiency (AATD)
24355919