ASPsiDb_ID | Mutant allele/ASP-siRNA | Mutant efficacy (%) |
Wild efficacy (%) |
Percentage discrimination (%) |
Gene | Disease | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|
ASPsiDb_ID | Mutant allele/ASP-siRNA | Mutant efficacy (%) |
Wild efficacy (%) |
Percentage discrimination (%) |
Gene | Disease | Analysis | Pubmed ID |
aspsirna0347 | AGCAGCAGCGGGACCUAUC UCGUCGUCGCCCUGGAUAG |
16 | 0 | 16 | Ataxin-3 (ATXN3) | Machado-Joseph disease (MJD)/Spinocerebellar ataxia type 3 (SCA3) | ![]() ![]() |