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siRNA Id: | aspsirna0979
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siRNA Name: | d9
|
Gene: | Ataxin-3 (ATXN3) |
Disease: | Parkinsons disease (PD) |
Wild allele/target (5'->3'): | NA
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Mutant allele/target (5'->3'): | CAGCAGCAGCAGCAGCAGCAGCAGCAG
|
Target Mutation: | c.209_211CAG(8_36),(p.Gln298_Gln305=)
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Wild siRNA (As strand): | NA
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ASP-siRNA (As strand): | GUCGUCGUCGUCGUCGUCGUCGUCGUC
|
Mismatch position in siRNA: | NA |
Mutant allele (5'->3'): | CAGCAGCAGCAGCAGCAGCAGCAGCAG
|
ASP-siRNA (As strand): | GUCGUCGUCGUCGUCGUCGUCGUCGUC
|
ASP-siRNA efficacy for mutant allele: | 78
|
Wild allele (5'->3'): | NA
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ASP-siRNA (As strand): | GUCGUCGUCGUCGUCGUCGUCGUCGUC
|
ASP-siRNA efficacy for wild allele: | 30
|
Percentage discrimination for ASP-siRNA: | 48
|
Wild allele (5'->3'): | NA
|
Wild siRNA (As strand): | NA
|
Wild sirna efficacy for wild allele: | NA
|
Wild allele (5'->3'): | NA
|
ASP-siRNA (As strand): | GUCGUCGUCGUCGUCGUCGUCGUCGUC
|
Wild sirna efficacy for mutant allele: | NA
|
Percentage discrimination for wild siRNA: | NA
|
Concentration: | 20nM |
Orientation: | Double strand |
Mismatch in: | siRNA |
UniProt ID: | P54252 |
Target sequence: | AGCAGCAAAAGCAGCAACAGCAGCAGCAGCAG |
Genbank Accesion: | NM_001164774.1 |
Cell-line: | Fibroblast |
Experimental technique used: | RT-PCR |
Transfection method: | Lipofectamine 2000 |
siRNA expression method: | Metabion |
Post-transfection duration: | 24 hours |
OMID ID: | 168600 |
KEGG disease ID: | H00056 |
Reference: | 21427085 |