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siRNA Id: | aspsirna2166
|
siRNA Name: | 618382
|
Gene: | Hungtintin (HTT) |
Disease: | Huntington disease (HD) |
Wild allele/target (5'->3'): | CAGCAGCAGCAGA
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Mutant allele/target (5'->3'): | UUCAGCUGCAGCAGA-P
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Target Mutation: | c.52CAG(36_39)
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Wild siRNA (As strand): | GUCGUCGUCGUCU
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ASP-siRNA (As strand): | GUCGACGUCGUCU-P
|
Mismatch position in siRNA: | A9U |
Mutant allele (5'->3'): | UUCAGCUGCAGCAGA-P
|
ASP-siRNA (As strand): | GUCGACGUCGUCU-P
|
ASP-siRNA efficacy for mutant allele: | 78
|
Wild allele (5'->3'): | CAGCAGCAGCAGA
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ASP-siRNA (As strand): | GUCGACGUCGUCU-P
|
ASP-siRNA efficacy for wild allele: | 21
|
Percentage discrimination for ASP-siRNA: | 57
|
Wild allele (5'->3'): | CAGCAGCAGCAGA
|
Wild siRNA (As strand): | GUCGUCGUCGUCU
|
Wild sirna efficacy for wild allele: | NA
|
Wild allele (5'->3'): | CAGCAGCAGCAGA
|
ASP-siRNA (As strand): | GUCGACGUCGUCU-P
|
Wild sirna efficacy for mutant allele: | NA
|
Percentage discrimination for wild siRNA: | NA
|
Concentration: | 25nM |
Orientation: | Antisense |
Mismatch in: | siRNA |
UniProt ID: | P42858 |
Target sequence: | CAGCAGCAGCAGCAGCAGCAGCAGCAGCAGCAGCAGCAGCAGCAGCAGCAGCA |
Genbank Accesion: | NM_002111.7 |
Cell-line: | GM04281/GM04869 |
Experimental technique used: | Western blot |
Transfection method: | RNAiMAX |
siRNA expression method: | Applied Biosystems |
Post-transfection duration: | 48 hours |
OMID ID: | 143100 |
KEGG disease ID: | H00059 |
Reference: | 24694346 |