Total number of Results for HD-human Embryonic Stem cells(hESCs) are 10
ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
ASPsiRNA ID Mutant allele/ASP-siRNA Efficacy
for mutant(%)
Efficacy
for wild (%)
Relative Difference (%) Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna3485 GGGACAGUAAUUCAACGCUU
CCCUGUCAUUAAGUUGCGAA
70 30 40 HTT Huntington disease (HD) NM_002111.7:c.5165C>A rs363125
24926995
aspsirna3486 GUAAUUCAACGCUAGAA
CAUUAAGUUGCGAUCUU
98 40 58 HTT Huntington disease (HD) NM_002111.7:c.5165C>A rs363125
24926995
aspsirna3487 GUACUUCAACGCUAGAAGAU
CAUGAAGUUGCGAUCUUCUA
88 20 68 HTT Huntington disease (HD) NM_002111.7:c.5165C>A rs363125
24926995
aspsirna3488 GGGACAGUACUUCAACGCUU
CCCUGUCAUGAAGUUGCGAA
97 67 30 HTT Huntington disease (HD) NM_002111.7:c.5165C>A rs363125
24926995
aspsirna3489 CCCUCAUCCACUGUGUGCA
GGGAGUAGGUGACACACGU
100 10 90 HTT Huntington disease (HD) NM_002111.7:c.6931T>C rs362331
24926995
aspsirna3490 CCCUCAUCUACUGUGUGCAU
GGGAGUAGAUGACACACGUA
75 40 35 HTT Huntington disease (HD) NM_002111.7:c.6931T>C rs362331
24926995
aspsirna3491 GUUUGAGCUAAUGUAUGUG
CAAACUCGAUUACAUACAC
60 0 60 HTT Huntington disease (HD) NM_002111.7:c.8163G>A rs2276881
24926995
aspsirna3492 GUUUGAGCUGAUGUAUGUGU
CAAACUCGACUACAUACACA
70 30 40 HTT Huntington disease (HD) NM_002111.7:c.8163G>A rs2276881
24926995
aspsirna3493 GGAAGUCUGCGCCCUUGUG
CCUUCAGACGCGGGAACAC
85 55 30 HTT Huntington disease (HD) NM_002111.6:c.9810C>T rs362307
24926995
aspsirna3494 GGAAGUCUGUGCCCUUGUGU
CCUUCAGACACGGGAACACA
82 60 22 HTT Huntington disease (HD) NM_002111.6:c.9810C>T rs362307
24926995