ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna1970 | AAAGGGUGAGCGUGGUCCA UUUCCCACUCGCACCAGGC |
60 | 40 | 20 | COL6A3 | Congenital muscular dystrophy type Ullrich (UCMD) | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1971 | CAAAGGGUGAGCGUGGUCA GUUUCCCACUCGCACCAGG |
40 | 30 | 10 | COL6A3 | Congenital muscular dystrophy type Ullrich (UCMD) | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1972 | CCAAAGGGUGAGCGUGGUA GGUUUCCCACUCGCACCAG |
65 | 35 | 30 | COL6A3 | Congenital muscular dystrophy type Ullrich (UCMD) | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1973 | GCCAAAGGGUGAGCGUGGG CGGUUUCCCACUCGCACCA |
59 | 30 | 29 | COL6A3 | Congenital muscular dystrophy type Ullrich (UCMD) | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1974 | GGCCAAAGGGUGAGCGUGA CCGGUUUCCCACUCGCACC |
70 | 25 | 45 | COL6A3 | Congenital muscular dystrophy type Ullrich (UCMD) | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1975 | GGGCCAAAGGGUGAGCGUU CCCGGUUUCCCACUCGCAC |
60 | 20 | 40 | COL6A3 | Congenital muscular dystrophy type Ullrich (UCMD) | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1976 | CGGGCCAAAGGGUGAGCGA GCCCGGUUUCCCACUCGCA |
78 | 50 | 28 | COL6A3 | Congenital muscular dystrophy type Ullrich (UCMD) | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1977 | UCGGGCCAAAGGGUGAGCA AGCCCGGUUUCCCACUCGC |
76 | 50 | 26 | COL6A3 | Congenital muscular dystrophy type Ullrich (UCMD) | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1978 | AUCGGGCCAAAGGGUGAGA UAGCCCGGUUUCCCACUCG |
80 | 54 | 26 | COL6A3 | Congenital muscular dystrophy type Ullrich (UCMD) | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1979 | CAUCGGGCCAAAGGGUGAA GUAGCCCGGUUUCCCACUC |
86 | 60 | 26 | COL6A3 | Congenital muscular dystrophy type Ullrich (UCMD) | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1980 | GCAUCGGGCCAAAGGGUGU CGUAGCCCGGUUUCCCACU |
90 | 58 | 32 | COL6A3 | Congenital muscular dystrophy type Ullrich (UCMD) | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |