| ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
|---|---|---|---|---|---|---|---|---|---|---|
| aspsirna1946 | GACCCCAGGCTCCACCAAA CUGGGGUCCGTGGUGGUUU |
80 | 14 | 66 | AAT | Emphysema/Alpha-1 antitrypsin deficiency (AATD) | c.1096G>A,p.Glu366Lys on M2,Glu342Lys on M1A | rs28929474 | 
|
|
| aspsirna1947 | GACCCCAGGCTCCACCAAA CUGGGGUCCGTGGUGGUUU |
80 | 14 | 66 | AAT | Emphysema/Alpha-1 antitrypsin deficiency (AATD) | c.1096G>A,p.Glu366Lys on M2,Glu342Lys on M1A | rs28929474 |
|
