ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna1794 | UCAAUGUGGCCAUGCAUGU AGUUACACCGGUACGUACA |
NA | 15 | NA | TTR | Familial amyloidotic polyneuropathy (FAP) | c.148G>A,p.Val50Met | rs28933979 | ![]() |