ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna0340 | GAGUGAUGCAGAAGAAGGG CUCACUACGUCUUCUUCCC |
85 | 10 | 75 | GNE | Sialuria | c.830G>A,p.Arg277Gln | rs12190862 | ![]() |