Total number of Results for ATXN1 are 6
ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
ASPsiRNA ID Mutant allele/ASP-siRNA Efficacy
for mutant(%)
Efficacy
for wild (%)
Relative Difference (%) Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna0701 CCAAGAAAGCCGAGAGCAU
GGUUCUUUCGGCUCUCGUC
0 24 -24 ATXN1 Spino Cerebellar Ataxia type-1 (SCA-1) c.589_591CAG(36_38),p.Gln208_His209 rs19392292
22397573
aspsirna0702 CAAGAAAGCCGAGAGCAGA
GUUCUUUCGGCUCUCGUCG
0 20 -20 ATXN1 Spino Cerebellar Ataxia type-1 (SCA-1) c.589_591CAG(36_38),p.Gln208_His209 rs19392292
22397573
aspsirna0703 AAGAAAGCCGAGAGCAGUA
UUCUUUCGGCUCUCGUCGG
58 32 26 ATXN1 Spino Cerebellar Ataxia type-1 (SCA-1) c.589_591CAG(36_38),p.Gln208_His209 rs19392292
22397573
aspsirna0704 AGCCGAGAGCAGCCGGCUU
UCGGCUCUCGUCGGCCGAC
47 78 -31 ATXN1 Spino Cerebellar Ataxia type-1 (SCA-1) c.589_591CAG(36_38),p.Gln208_His209 rs19392292
22397573
aspsirna0972 CAGCAGCAGCAGCAGCAGCAG
GUCGUCGUCGUCGUCGUCGUC
50 39 11 ATXN1 Spino Cerebellar Ataxia type-1 (SCA-1) c.589_591CAG(36_38) rs19392292
21427085
aspsirna0978 CAGCAGCAGCAGCAGCAGCAGCAGCAG
GUCGUCGUCGUCGUCGUCGUCGUCGUC
56 39 17 ATXN1 Neurological disorder c.589_591CAG(36_38) rs19392292
21427085