ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
ASPsiRNA ID | Mutant allele/ASP-siRNA | Efficacy for mutant(%) |
Efficacy for wild (%) |
Relative Difference (%) | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
aspsirna0701 | CCAAGAAAGCCGAGAGCAU GGUUCUUUCGGCUCUCGUC |
0 | 24 | -24 | ATXN1 | Spino Cerebellar Ataxia type-1 (SCA-1) | c.589_591CAG(36_38),p.Gln208_His209 | rs19392292 | ![]() |
|
aspsirna0702 | CAAGAAAGCCGAGAGCAGA GUUCUUUCGGCUCUCGUCG |
0 | 20 | -20 | ATXN1 | Spino Cerebellar Ataxia type-1 (SCA-1) | c.589_591CAG(36_38),p.Gln208_His209 | rs19392292 | ![]() |
|
aspsirna0703 | AAGAAAGCCGAGAGCAGUA UUCUUUCGGCUCUCGUCGG |
58 | 32 | 26 | ATXN1 | Spino Cerebellar Ataxia type-1 (SCA-1) | c.589_591CAG(36_38),p.Gln208_His209 | rs19392292 | ![]() |
|
aspsirna0704 | AGCCGAGAGCAGCCGGCUU UCGGCUCUCGUCGGCCGAC |
47 | 78 | -31 | ATXN1 | Spino Cerebellar Ataxia type-1 (SCA-1) | c.589_591CAG(36_38),p.Gln208_His209 | rs19392292 | ![]() |
|
aspsirna0972 | CAGCAGCAGCAGCAGCAGCAG GUCGUCGUCGUCGUCGUCGUC |
50 | 39 | 11 | ATXN1 | Spino Cerebellar Ataxia type-1 (SCA-1) | c.589_591CAG(36_38) | rs19392292 | ![]() |
|
aspsirna0978 | CAGCAGCAGCAGCAGCAGCAGCAGCAG GUCGUCGUCGUCGUCGUCGUCGUCGUC |
56 | 39 | 17 | ATXN1 | Neurological disorder | c.589_591CAG(36_38) | rs19392292 | ![]() |