| ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
|---|---|---|---|---|---|---|---|---|---|---|
| ASPsiRNA ID | Mutant allele/ASP-siRNA | Efficacy for mutant(%) |
Efficacy for wild (%) |
Relative Difference (%) | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
| aspsirna0559 | GCUCUUCUCCUUCUUAACU CGAGAAGAGGAAGAAUUGA |
34 | 22 | 12 | CHRNA1 | Congenital myasthenic syndrome (SCCMS) | c.737C>T,p.Ser271Phe | rs48335304 | 
|
|
| aspsirna0564 | GCUCUUCUUCUUCUUAACU CGAGAAGAAGAAGAAUUGA |
Low efficacy | High efficacy | High discrimination | CHRNA1 | Congenital myasthenic syndrome (SCCMS) | c.737C>T,p.Ser271Phe | rs48335304 |
|