Total number of Results for 11C are 2
ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
ASPsiRNA ID Mutant allele/ASP-siRNA Efficacy
for mutant(%)
Efficacy
for wild (%)
Relative Difference (%) Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna2214 CAGCAGCAUCAGCAGCAGC
GUCGUCGUUGUCGUCGUCG
96 43 53 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2217 CAGCAGCAUCAGCAGCAGC
GUCGUCGUUGUCGUCGUCG
98 34 64 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774