ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna1209 | CUUAUGGGAGAGAGCACG GAAUACCCUCUCUCGUGC |
2 | 38 | -36 | CD46 | Hemolytic uremic syndrome | NM_002389.4:c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |
|
aspsirna1263 | CUUAUGGGAGAGAGCACGA GAAUACCCUCUCUCGUGCU |
14 | 10 | 4 | CD46 | Hemolytic uremic syndrome | NM_002389.4:c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |