ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna1340 | CUUAUUGGAGAGAGCACGA GAAUAACCUCUCUCGUGCU |
42 | 40 | 2 | CD46 | Hemolytic uremic syndrome | NM_002389.4:c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |
|
aspsirna1743 | AGUCUCUGUAGGAGUAUUA UCAGAGACAUCCUCAUAAU |
78 | 56 | 22 | CD46 | Hemolytic uremic syndrome | NM_002389.4:c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |