ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna3024 | CACUAGUAGUAACUAUAAU GUGAUCAUCAUUGAUAUUA |
15 | 8 | 7 | SNCA | Parkinsons disease (PD) | SNCA locus triplication | NA | ![]() |