| ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
|---|---|---|---|---|---|---|---|---|---|---|
| aspsirna2146 | GCAGCAGCUGCAGCAGA-VP CGUCGUCGACGUCGUCU-VP |
70 | 10 | 60 | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs19392295 | 
|
|
| aspsirna3618 | UCAGAGAGAUCCUCAUAAA AGUCUCUCAAGGAGUAUUU |
90 | 0 | 90 | PPIB/Cyclophilin B | PPIB-Related Osteogenesis Imperfecta (Type IX) | NA | NA |
|
