ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna2014 | UUUAUGAUGAUCUCUCUGA AAAUACUACUAGAGAGACU |
85 | 30 | 55 | P. luciferase | NA | NA | NA | ![]() |
|
aspsirna2071 | CUCUCCUUUAGCUAAGGCC GAGAGGAAAUCGAUUCCGG |
50 | 45 | 5 | PPIB/Cyclophilin B | NA | NA | NA | ![]() |
|
aspsirna2107 | GAGCUGUUGGCGUAGGCAA CUCGACAACCGCAUCCGUU |
5 | 20 | -15 | KRAS | Cancer | c.35G>T,p.Gly12Val | rs12191352 | ![]() |
|
aspsirna2128 | GAGCUGUUGGCGUAGGCAA CUCGACAACCGCAUCCGUU |
5 | 20 | -15 | KRAS | Cancer | c.35G>T,p.Gly12Val | rs12191352 | ![]() |
|
aspsirna0355 | AUCAAAGUUCCAGCUGGGA UAGUUUCAAGGUCGACCCU |
82 | 0 | 82 | COL3A1 | Vascular Ehlers-Danlos Syndrome (vEDs) | c.764G>T,p.Gly255Val | rs58777960 | ![]() |
|
aspsirna0070 | AGUGAUCUUCAUCACCUUG UCACUAGAAGUAGUGGAAC |
10 | 16 | -6 | APP | Alzheimers disease | c.2010_2011delGAinsTC (p.Lys670_Met671delinsAsnLeu) | rs28186516 | ![]() |
|
aspsirna3622 | UCAGAGAGAUCCUCAUAAA AGUCUCUAUAGGAGUAUUU |
90 | 0 | 90 | PPIB/Cyclophilin B | PPIB-Related Osteogenesis Imperfecta (Type IX) | NA | NA | ![]() |
|
aspsirna3698 | GGUUGGAGGAGAGAUGAUA CCAACCUACUCUCUACUAU |
90 | 55 | 35 | PPIB/Cyclophilin B | PPIB-Related Osteogenesis Imperfecta (Type IX) | NA | NA | ![]() |