ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna2077 | CUCUCUUGUAGCUAAGGCC GAGAGAACAUCGAUUCCGG |
86 | 45 | 41 | PPIB/Cyclophilin B | NA | NA | NA | ![]() |
|
aspsirna2445 | AACUCUUCCGCGCAACUUU UUGAGAAGGCGCGUUGAAA |
0 | 70 | -70 | KRAS | NA | NA | NA | ![]() |
|
aspsirna3139 | AGGCCUGGAUCUGUGCUUG UCCGGACCUAGACACGAAC |
40 | 18 | 22 | TP63 | Ectrodactily-ectodermal dysplasia and cleft lip/palate (EEC) | c.727C>T, p.Arg243Trp | rs12190883 | ![]() |
|
aspsirna3288 | CUGCUCCCUCAUCUACUGUGU GACGAGGGAGUAGAUGACACA |
10 | 2 | 8 | HTT | Huntington disease (HD) | NM_002111.7:c.6931T>C | rs362331 | ![]() |
|
aspsirna3309 | CUUUGGAAGUCUGUGCCCUUG GAAACCUUCAGACACGGGAAC |
60 | 45 | 15 | HTT | Huntington disease (HD) | NM_002111.6:c.9810C>T | rs362307 | ![]() |
|
aspsirna3060 | CGGACUGCACGGAGAAGCU GCCUGACGUGCCUCUUCGA |
60 | 20 | 40 | TGFBI | Lattice corneal dystrophy type I (LCDI) | c.370C>T,p.Arg124Cys | rs12190921 | ![]() |
|
aspsirna3067 | CGGACUGCACGGAGAAGCU GCCUGACGUGCCUCUUCGA |
50 | 10 | 40 | TGFBI | Lattice corneal dystrophy type I (LCDI) | c.370C>T,p.Arg124Cys | rs12190921 | ![]() |
|
aspsirna3069 | CGGACUGCACGGAGAAGCU GCCUGACGUGCCUCUUCGA |
50 | 10 | 40 | TGFBI | Lattice corneal dystrophy type I (LCDI) | c.370C>T,p.Arg124Cys | rs12190921 | ![]() |
|
aspsirna0589 | AUUCUUGGCUGGCCUCUUA UAAGAACCGACCGGAGAAU |
54 | 0 | 54 | KRT9 | Epidermolytic palmoplantar keratoderma (EPPK) | c.487C>T,p.Arg163Trp | rs59616921 | ![]() |