ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna3369 | CCUUUGGAAGUCUAUGCCCUU GGAAACCUUCAGAUACGGGAA |
31 | 22 | 9 | HTT | Huntington disease (HD) | NM_002111.6:c.9810C>T | rs362307 | ![]() |