ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna3382 | ACUUUGGAAGUCUGUGCCCUU UGAAACCUUCAGACACGGGAA |
60 | 22 | 38 | HTT | Huntington disease (HD) | NM_002111.6:c.9810C>T | rs362307 | ![]() |