ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna2086 | CUUUCCUGUAGCUAAGGCC GAAAGGACAUCGAUUCCGG |
76 | 45 | 31 | PPIB/Cyclophilin B | NA | NA | NA | ![]() |
|
aspsirna2454 | AAUUCCUCCGCGCAACUUU UUAAGGAGGCGCGUUGAAA |
5 | 70 | -65 | KRAS | NA | NA | NA | ![]() |
|
aspsirna3136 | CCUGGAUCUGUGCUUGCCC GGACCUAGACACGAACGGG |
50 | 43 | 7 | TP63 | Ectrodactily-ectodermal dysplasia and cleft lip/palate (EEC) | c.727C>T, p.Arg243Trp | rs12190883 | ![]() |
|
aspsirna3285 | CGCCUGCUCCCUCAUCUACUG GCGGACGAGGGAGUAGAUGAC |
35 | 20 | 15 | HTT | Huntington disease (HD) | NM_002111.7:c.6931T>C | rs362331 | ![]() |
|
aspsirna3306 | AGCCUUUGGAAGUCUGUGCCC UCGGAAACCUUCAGACACGGG |
33 | 0 | 33 | HTT | Huntington disease (HD) | NM_002111.6:c.9810C>T | rs362307 | ![]() |
|
aspsirna3063 | ACUGCACGGAGAAGCUGAG UGACGUGCCUCUUCGACUC |
45 | 40 | 5 | TGFBI | Lattice corneal dystrophy type I (LCDI) | c.370C>T,p.Arg124Cys | rs12190921 | ![]() |
|
aspsirna0592 | CUUGGCUGGCCUCUUACUU GAACCGACCGGAGAAUGAA |
60 | 0 | 60 | KRT9 | Epidermolytic palmoplantar keratoderma (EPPK) | c.487C>T,p.Arg163Trp | rs59616921 | ![]() |
|
aspsirna1013 | CCUCAAAAGCCAAAAAAUG GGAGUUUUCGGUUUUUUAC |
78 | 44 | 34 | COL1A1 | Osteogenesis Imperfecta (OI) | c.*88T>C | rs1061237 | ![]() |
|
aspsirna1016 | CCUCAAAAGCCAAAAAAUG GGAGUUUUCGGUUUUUUAC |
78 | 44 | 34 | COL1A1 | Osteogenesis Imperfecta (OI) | c.*88T>C | rs1061237 | ![]() |