| ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
|---|---|---|---|---|---|---|---|---|---|---|
| aspsirna2041 | CUCUCCUGUAGCUAAGGUC GAGAGGACAUCGAUUCCAG |
80 | 45 | 35 | PPIB/Cyclophilin B | NA | NA | NA | 
|
|
| aspsirna3151 | GACGCUGCUUUGAGGCCUG CUGCGACGAAACUCCGGAC |
37 | 10 | 27 | TP63 | Ectrodactily-ectodermal dysplasia and cleft lip/palate (EEC) | c.727C>T, p.Arg243Trp | rs12190883 |
|
|
| aspsirna3300 | CUACUGUGUGCACUUCAUCCU GAUGACACACGUGAAGUAGGA |
62 | 55 | 7 | HTT | Huntington disease (HD) | NM_002111.7:c.6931T>C | rs362331 |
|
|
| aspsirna3321 | GUGCCCUUGUGCCCUCCACCG CACGGGAACACGGGAGGUGGC |
10 | 0 | 10 | HTT | Huntington disease (HD) | NM_002111.6:c.9810C>T | rs362307 |
|
|
| aspsirna3048 | CUCAGCUGUACACGGACUG GAGUCGACAUGUGCCUGAC |
20 | 10 | 10 | TGFBI | Lattice corneal dystrophy type I (LCDI) | c.370C>T,p.Arg124Cys | rs12190921 |
|
|
| aspsirna0577 | UGCAGGAACUCAAUUCUUG ACGUCCUUGAGUUAAGAAC |
15 | 22 | -7 | KRT9 | Epidermolytic palmoplantar keratoderma (EPPK) | c.487C>T,p.Arg163Trp | rs59616921 |
|
|
| aspsirna0806 | CGGAGCCUUUGGAAGUCUGUA GCCUCGGAAACCUUCAGACAU |
78 | 22 | 56 | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs362307 |
|
