| ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
|---|---|---|---|---|---|---|---|---|---|---|
| aspsirna3150 | ACGCUGCUUUGAGGCCUGG UGCGACGAAACUCCGGACC |
3 | 0 | 3 | TP63 | Ectrodactily-ectodermal dysplasia and cleft lip/palate (EEC) | c.727C>T, p.Arg243Trp | rs12190883 | 
|
|
| aspsirna3299 | UCUACUGUGUGCACUUCAUCC AGAUGACACACGUGAAGUAGG |
30 | 12 | 18 | HTT | Huntington disease (HD) | NM_002111.7:c.6931T>C | rs362331 |
|
|
| aspsirna3320 | UGUGCCCUUGUGCCCUCCACC ACACGGGAACACGGGAGGUGG |
30 | 20 | 10 | HTT | Huntington disease (HD) | NM_002111.6:c.9810C>T | rs362307 |
|
|
| aspsirna3049 | UCAGCUGUACACGGACUGC AGUCGACAUGUGCCUGACG |
45 | 40 | 5 | TGFBI | Lattice corneal dystrophy type I (LCDI) | c.370C>T,p.Arg124Cys | rs12190921 |
|
|
| aspsirna0578 | GCAGGAACUCAAUUCUUGG CGUCCUUGAGUUAAGAACC |
20 | 0 | 20 | KRT9 | Epidermolytic palmoplantar keratoderma (EPPK) | c.487C>T,p.Arg163Trp | rs59616921 |
|
|
| aspsirna0616 | UAAUGAGAAGAGCACCGUG AUUACUCUUCUCGUGGCAC |
0 | 18 | -18 | KRT9 | Epidermolytic palmoplantar keratoderma (EPPK) | c.469A>G ,p.Met157Val | rs58597584 |
|
|
| aspsirna0807 | GGAGCCUUUGGAAGUCUGUGA CCUCGGAAACCUUCAGACACU |
65 | 47 | 18 | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs362307 |
|
