ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna0986 | UAGCAGCAGCAGCAGCAGUAG AUCGUCGUCGUCGUCGUCAUC |
60 | 45 | 15 | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs19392295 | ![]() |
|
aspsirna0990 | UAGCAGCAGCAGCAGCAGUAG AUCGUCGUCGUCGUCGUCAUC |
60 | 45 | 15 | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs19392295 | ![]() |