ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna2047 | CUCUCCUGUAGCUAAUGCC GAGAGGACAUCGAUUACGG |
72 | 45 | 27 | PPIB/Cyclophilin B | NA | NA | NA | ![]() |
|
aspsirna2098 | UGGUAGUUGGAGCUGUUGG ACCAUCAACCUCGACAACC |
5 | 0 | 5 | KRAS | Cancer | c.35G>T,p.Gly12Val | rs12191352 | ![]() |
|
aspsirna2119 | UGGUAGUUGGAGCUGUUGG ACCAUCAACCUCGACAACC |
5 | 0 | 5 | KRAS | Cancer | c.35G>T,p.Gly12Val | rs12191352 | ![]() |
|
aspsirna1886 | UCUCCUGGUGAAGCUUGUC AGAGGACCACUUCGAACAG |
40 | 22 | 18 | COL1A1 | Osteogenesis Imperfecta (OI) | c.3244G>T,p.Gly1082Cys | rs72656303 | ![]() |
|
aspsirna0363 | CUCCAGGUAUCAAAGUUCC GAGGUCCAUAGUUUCAAGG |
20 | 4 | 16 | COL3A1 | Vascular Ehlers-Danlos Syndrome (vEDs) | c.764G>T,p.Gly255Val | rs58777960 | ![]() |
|
aspsirna3666 | GGUUGGAGGAGAGAUGAUA CCAACCUCCUCUCUAAUAU |
90 | 58 | 32 | PPIB/Cyclophilin B | PPIB-Related Osteogenesis Imperfecta (Type IX) | NA | NA | ![]() |