ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna3349 | AUCUACUGUGUGCAAUUCAUC UAGAUGACACACGUUAAGUAG |
90 | 30 | 60 | HTT | Huntington disease (HD) | NM_002111.7:c.6931T>C | rs362331 | ![]() |
|
aspsirna3431 | AUCUACUGUGUGCAAUUCAUC UAGAUGACACACGUUAAGUAG |
50 | 20 | 30 | HTT | Huntington disease (HD) | NM_002111.7:c.6931T>C | rs362331 | ![]() |
|
aspsirna3432 | AUCUACUGUGUGCAAUUCAUC UAGAUGACACACGUUAAGUAG |
55 | 15 | 40 | HTT | Huntington disease (HD) | NM_002111.7:c.6931T>C | rs362331 | ![]() |
|
aspsirna3433 | AUCUACUGUGUGCAAUUCAUC UAGAUGACACACGUUAAGUAG |
55 | 0 | 55 | HTT | Huntington disease (HD) | NM_002111.7:c.6931T>C | rs362331 | ![]() |
|
aspsirna3434 | AUCUACUGUGUGCAAUUCAUC UAGAUGACACACGUUAAGUAG |
60 | 0 | 60 | HTT | Huntington disease (HD) | NM_002111.7:c.6931T>C | rs362331 | ![]() |