ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna2100 | GUAGUUGGAGCUGUUGGCG CAUCAACCUCGACAACCGC |
3 | 0 | 3 | KRAS | Cancer | c.35G>T,p.Gly12Val | rs12191352 | ![]() |
|
aspsirna2121 | GUAGUUGGAGCUGUUGGCG CAUCAACCUCGACAACCGC |
3 | 0 | 3 | KRAS | Cancer | c.35G>T,p.Gly12Val | rs12191352 | ![]() |
|
aspsirna1888 | UCCUGGUGAAGCUUGUCGU AGGACCACUUCGAACAGCA |
52 | 40 | 12 | COL1A1 | Osteogenesis Imperfecta (OI) | c.3244G>T,p.Gly1082Cys | rs72656303 | ![]() |
|
aspsirna0361 | CCAGGUAUCAAAGUUCCAG GGUCCAUAGUUUCAAGGUC |
3 | 3 | 0 | COL3A1 | Vascular Ehlers-Danlos Syndrome (vEDs) | c.764G>T,p.Gly255Val | rs58777960 | ![]() |
|
aspsirna3751 | AAAGUUGCGCGGAGGAGUU UUUCAACGCGCCUACUCAA |
90 | 38 | 52 | PPIB/Cyclophilin B | PPIB-Related Osteogenesis Imperfecta (Type IX) | NA | NA | ![]() |