Total number of Results for A6U are 11
Search:
ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna2053 CUCUCCUGUAGCUUAGGCC
GAGAGGACAUCGAAUCCGG
85 45 40 PPIB/Cyclophilin B NA NA NA
US2005/0176045A1
aspsirna2421 AACUCCUCCGCGCUACUUU
UUGAGGAGGCGCGAUGAAA
83 70 13 KRAS NA NA NA
US007576197B2
aspsirna2232 UUCAGCAGCAGCAGCUGCAGU
AAGUCGUCGUCGUCGACGUCU
30 10 20 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna0664 AAGUCCUUCCAGCUGCAGC
UUCAGGAAGGUCGACGUCG
5 11 -6 HTT Huntington disease (HD) c.52CAG(36_39) rs19392295
23042244
aspsirna3029 CAGCAGCAGCAGCUGCAGC
GUCGUCGUCGUCGACGUCG
35 30 5 ATXN3 Machado-Joseph Disease (MJD)/Spinocerebellar ataxia type 3 (SCA3) c.892_894CAG(8_36) (p.Gln298_Gln305=) rs19392292
21294677
aspsirna0777 CAGCAGCAGCAGCUGCAGC
GUCGUCGUCGUCGACGUCG
20 90 -70 HTT Huntington disease (HD) c.52CAG(36_39) rs19392295
21095568
aspsirna0110 CGAGUAAGCUAAAUACCAA
GCUCAUUCGAUUUAUGGUU
82 99 -17 PRNP Prion disease/Gerstmann-Straussler disease c.314C>T,p.Pro105Leu rs11538758
18493311
aspsirna0149 CGAGUAAGCUAAAUACCAA
GCUCAUUCGAUUUAUGGUU
82 99 -17 PRNP Prion disease/Gerstmann-Straussler disease c.314C>T,p.Pro105Leu rs11538758
18493311
aspsirna0901 AAGGAGGGAGCUUCUCUCA
UUCCUCCCUCGAAGAGAGU
30 NA NA HLA-A heavy chain HLA incompatibility c.*66A>T rs1061235
16520945
aspsirna0913 AAGGAGGGAGCUUCUCUCA
UUCCUCCCUCGAAGAGAGU
35 NA NA HLA-A heavy chain HLA incompatibility c.*66A>T rs1061235
16520945
aspsirna3674 GGUUGGAGGAGAGAUGAUA
CCAACCUCCUCUCAACUAU
90 85 5 PPIB/Cyclophilin B PPIB-Related Osteogenesis Imperfecta (Type IX) NA NA
16489337
Showing 1 to 11 of 11 entries