| ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
|---|---|---|---|---|---|---|---|---|---|---|
| aspsirna0108 | CGAGUAAGCUAUAAACCAA GCUCAUUCGAUAUUUGGUU |
67 | 99 | -32 | PRNP | Prion disease/Gerstmann-Straussler disease | c.314C>T,p.Pro105Leu | rs11538758 | 
|
|
| aspsirna0147 | CGAGUAAGCUAUAAACCAA GCUCAUUCGAUAUUUGGUU |
67 | 99 | -32 | PRNP | Prion disease/Gerstmann-Straussler disease | c.314C>T,p.Pro105Leu | rs11538758 |
|
|
| aspsirna3682 | GGUUGGAGGAGAGAUGAUA CCAACCUCCUCACUACUAU |
90 | 62 | 28 | PPIB/Cyclophilin B | PPIB-Related Osteogenesis Imperfecta (Type IX) | NA | NA |
|
