ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna0118 | GGAACAAGCUGUGUAAGCC CCUUGUUCGACACAUUCGG |
70 | 90 | -20 | PRNP | Prion disease/Gerstmann-Straussler disease | c.305C>T,p.Pro102Leu | rs74315401 | ![]() |
|
aspsirna0154 | GGAACAAGCUGUGUAAGCC CCUUGUUCGACACAUUCGG |
70 | 90 | -20 | PRNP | Prion disease/Gerstmann-Straussler disease | c.305C>T,p.Pro102Leu | rs74315401 | ![]() |