Total number of Results for A8U,U11C are 1
ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
ASPsiRNA ID Mutant allele/ASP-siRNA Efficacy
for mutant(%)
Efficacy
for wild (%)
Relative Difference (%) Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna0368 AGUGGCUCACCUGAUUACA
UCACCGAGUGGACUAAUGU
80 17 63 ACVR1 Fibrodysplasia Ossificans Progressiva (FOP) c.617G>A,p.Arg206His rs12191267
22130450