| ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
|---|---|---|---|---|---|---|---|---|---|---|
| aspsirna2205 | AACAGCAGCAGUUGCAGCAGC UUGUCGUCGUCAACGUCGUCG |
83 | 15 | 68 | ATN-1 | Dentatorubral-pallidoluysian atrophy (DRPLA) | c.1462_1464CAG(90_93) | rs19392293 | 
|
|
| aspsirna2240 | UUCAGCAGCAGUUGCAGCAGU AAGUCGUCGUCAACGUCGUCU |
67 | 25 | 42 | ATN-1 | Dentatorubral-pallidoluysian atrophy (DRPLA) | c.1462_1464CAG(90_93) | rs19392293 |
|
|
| aspsirna0662 | CAGCAGCAGUUGCAGCAGC GUCGUCGUCAACGUCGUCG |
58 | 22 | 36 | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs19392295 |
|
|
| aspsirna0787 | CAGCAGCAGUUGCAGCAGC GUCGUCGUCAACGUCGUCG |
60 | 20 | 40 | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs19392295 |
|
