| ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
|---|---|---|---|---|---|---|---|---|---|---|
| aspsirna2243 | UUCAGCAGCAUCUGCAGCAGU AAGUCGUCGUAGACGUCGUCU |
80 | 45 | 35 | ATN-1 | Dentatorubral-pallidoluysian atrophy (DRPLA) | c.1462_1464CAG(90_93) | rs19392293 | 
|
|
| aspsirna2148 | CAGCAGCAUCUGCAGCAGU-P GUCGUCGUAGACGUCGUCU-P |
90 | 20 | 70 | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs19392295 |
|
