Total number of Results for A9U,A17C are 1
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ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna2154 CAUCAGCAGCUGCAGCAGU-VP
GUAGUCGUCGACGUCGUCU-VP
78 5 73 HTT Huntington disease (HD) c.52CAG(36_39) rs19392295
24694346
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