ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna2155 | CUGCAGCAGCUGCAGCAGU-P GACGUCGUCGACGUCGUCU-P |
60 | 30 | 30 | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs19392295 | ![]() |
|
aspsirna2157 | CUGCAGCAGCUGCAGCAGU-VP GACGUCGUCGACGUCGUCU-VP |
50 | 45 | 5 | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs19392295 | ![]() |