ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna2342 | AGUGUAACGUGUUCAGAGG UCACAUUGCCCAAGUCUCC |
65 | NA | NA | SOD1 | Amyotrophic Lateral Sclerosis (ALS) | c.256G>C,p.Gly86Arg | rs12191243 | ![]() |
|
aspsirna1803 | CUUAUUUGAGAGAGCACGA GAAUAACCUCUCUCGUGCU |
0 | 93 | 93 | CD46 | Hemolytic uremic syndrome | c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |
|
aspsirna1807 | CUUAUUGUAGAGAGCACGA GAAUAACCUCUCUCGUGCU |
25 | 93 | 68 | CD46 | Hemolytic uremic syndrome | c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |
|
aspsirna1815 | CUUAUUGGAUAGAGCACGA GAAUAACCUCUCUCGUGCU |
0 | 93 | 93 | CD46 | Hemolytic uremic syndrome | c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |
|
aspsirna1823 | CUUAUUGGAGAUAGCACGA GAAUAACCUCUCUCGUGCU |
56 | 93 | 37 | CD46 | Hemolytic uremic syndrome | c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |
|
aspsirna1832 | CUUAUUGGAGAGAUCACGA GAAUAACCUCUCUCGUGCU |
62 | 93 | 31 | CD46 | Hemolytic uremic syndrome | c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |
|
aspsirna1847 | CUUAUUGGAGAGAGCACUA GAAUAACCUCUCUCGUGCU |
90 | 93 | 3 | CD46 | Hemolytic uremic syndrome | c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |