Total number of Results for C12A are 2
ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
ASPsiRNA ID Mutant allele/ASP-siRNA Efficacy
for mutant(%)
Efficacy
for wild (%)
Relative Difference (%) Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna0075 GUGAUCGGCAUCACCUUGG
CACUAGCCGUAGUGGAACC
12 8 4 APP Alzheimers disease c.2010_2011delGAinsTC (p.Lys670_Met671delinsAsnLeu) rs28186516
19771217
aspsirna0940 AUGUCCUGCCAGCAGCUGC
UACAGGACGGUCGUCGACG
82 23 59 AR Spinal and Bulbar Muscular Atrophy, X-linked 1; SMAX1/Kennedy’s disease c.172_174CAG(10_36) (p.Gln69_Gln80del)] rs19392293
11809726