Total number of Results for C13A are 3
ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
ASPsiRNA ID Mutant allele/ASP-siRNA Efficacy
for mutant(%)
Efficacy
for wild (%)
Relative Difference (%) Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna0941 AUGUCCGUCCAGCUGCAGC
UACAGGCAGGUCGACGUCG
40 20 20 AR Spinal and Bulbar Muscular Atrophy, X-linked 1; SMAX1/Kennedy’s disease c.172_174CAG(10_36) (p.Gln69_Gln80del)] rs19392293
11809726
aspsirna2074 CUCUCCGGUAGCUAAGGCC
GAGAGGCCAUCGAUUCCGG
72 45 27 PPIB/Cyclophilin B NA NA NA
US2005/0176045A1
aspsirna2442 AACUCCGCCGCGCAACUUU
UUGAGGCGGCGCGUUGAAA
50 70 -20 KRAS NA NA NA
US007576197B2