ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna2074 | CUCUCCGGUAGCUAAGGCC GAGAGGCCAUCGAUUCCGG |
72 | 45 | 27 | PPIB/Cyclophilin B | NA | NA | NA | ![]() |
|
aspsirna2442 | AACUCCGCCGCGCAACUUU UUGAGGCGGCGCGUUGAAA |
50 | 70 | -20 | KRAS | NA | NA | NA | ![]() |
|
aspsirna0941 | AUGUCCGUCCAGCUGCAGC UACAGGCAGGUCGACGUCG |
40 | 20 | 20 | AR | Spinal and Bulbar Muscular Atrophy, X-linked 1; SMAX1/Kennedy’s disease | c.172_174CAG(10_36) (p.Gln69_Gln80del)] | rs19392293 | ![]() |