ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna0478 | GCAGAAGAAGGUUCUGGAC CGUCUUCUUCCAAGACCUG |
30 | 0 | 30 | KRT5 | Epidermolysis bullosa simplex (EBS) | c.579C>G, p.Asn193Lys | rs60586163 | ![]() |
|
aspsirna0516 | GCAGAAGAAGGUUCUGGAC CGUCUUCUUCCAAGACCUG |
30 | 0 | 30 | KRT5 | Epidermolysis bullosa simplex (EBS) | c.579C>G, p.Asn193Lys | rs60586163 | ![]() |
|
aspsirna0434 | AGUGUUGUGGUUGGUAAAG UCACAACACCAACCAUUUC |
73 | 40 | 33 | PSEN1 | Alzheimers disease | c.811C>G, p.Leu271Val | rs63750886 | ![]() |