ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna2078 | CUCUCGUGUAGCUAAGGCC GAGAGCACAUCGAUUCCGG |
90 | 45 | 45 | PPIB/Cyclophilin B | NA | NA | NA | ![]() |
|
aspsirna2446 | AACUCGUCCGCGCAACUUU UUGAGCAGGCGCGUUGAAA |
8 | 70 | -62 | KRAS | NA | NA | NA | ![]() |
|
aspsirna0479 | CAGAAGAAGGUUCUGGACA GUCUUCUUCCAAGACCUGU |
25 | 0 | 25 | KRT5 | Epidermolysis bullosa simplex (EBS) | c.579C>G, p.Asn193Lys | rs60586163 | ![]() |
|
aspsirna0517 | CAGAAGAAGGUUCUGGACA GUCUUCUUCCAAGACCUGU |
25 | 0 | 25 | KRT5 | Epidermolysis bullosa simplex (EBS) | c.579C>G, p.Asn193Lys | rs60586163 | ![]() |
|
aspsirna0433 | GUGUUGUGGUUGGUAAAGC CACAACACCAACCAUUUCG |
90 | 15 | 75 | PSEN1 | Alzheimers disease | c.811C>G, p.Leu271Val | rs63750886 | ![]() |