ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna0628 | CACCGUGCAGGAACUCAAU GUGGCACGUCCUUGAGUUA |
90 | 42 | 48 | KRT9 | Epidermolytic palmoplantar keratoderma (EPPK) | c.469A>G ,p.Met157Val | rs58597584 | ![]() |
|
aspsirna3635 | UCAGAGAGAUCCUCAUAAA AGUCCCUCUAGGAGUAUUU |
90 | 81 | 9 | PPIB/Cyclophilin B | PPIB-Related Osteogenesis Imperfecta (Type IX) | NA | NA | ![]() |