ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna2406 | AACUCCUCCGCGCAACUUG UUGAGGAGGCGCGUUGAAC |
90 | 70 | 20 | KRAS | NA | NA | NA | ![]() |
|
aspsirna1953 | GGGCCAAAGGGUGAGCGUG CCCGGUUUCCCACUCGCAC |
NA | NA | 40 | COL6A3 | Dominant ullrich muscular dystrophy | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1964 | GGGCCAAAGGGUGAGCGUG CCCGGUUUCCCACUCGCAC |
NA | NA | 43 | COL6A3 | Dominant ullrich muscular dystrophy | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1975 | GGGCCAAAGGGUGAGCGUU CCCGGUUUCCCACUCGCAC |
60 | 20 | 40 | COL6A3 | Congenital muscular dystrophy type Ullrich (UCMD) | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna3731 | AAAGUUGCGCGGAGGAGUU UUUCAACGCGCCUCCUCAC |
90 | 66 | 24 | PPIB/Cyclophilin B | PPIB-Related Osteogenesis Imperfecta (Type IX) | NA | NA | ![]() |