| ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
|---|---|---|---|---|---|---|---|---|---|---|
| aspsirna2039 | CUCUCCUGUAGCUAAGGCG GAGAGGACAUCGAUUCCGC |
78 | 45 | 33 | PPIB/Cyclophilin B | NA | NA | NA | 
|
|
| aspsirna0466 | GUUCCUGGAGCAGCAGAAG CAAGGACCUCGUCGUCUUC |
45 | 0 | 45 | KRT5 | Epidermolysis bullosa simplex (EBS) | c.579C>G, p.Asn193Lys | rs60586163 |
|
|
| aspsirna0504 | GUUCCUGGAGCAGCAGAAG CAAGGACCUCGUCGUCUUC |
45 | 0 | 45 | KRT5 | Epidermolysis bullosa simplex (EBS) | c.579C>G, p.Asn193Lys | rs60586163 |
|
|
| aspsirna0446 | UUCAUUUUCUACAGUGUUG AAGUAAAAGAUGUCACAAC |
70 | 0 | 70 | PSEN1 | Alzheimers disease | c.811C>G, p.Leu271Val | rs63750886 |
|
|
| aspsirna1831 | AAGCAGCACAAUGAUGAGUGG UUCGUCGUGUUACUACUCACC |
NA | 72 | NA | Fen1 | Werner syndrome | NA | NA |
|
|
| aspsirna0937 | AUGACGACGCUGGUAUAGG UACUGCUGCGACCAUAUCC |
73 | 33 | 40 | AR | Spinal and Bulbar Muscular Atrophy, X-linked 1; SMAX1/Kennedy’s disease | c.172_174CAG(10_36) (p.Gln69_Gln80del)] | rs19392293 |
|
|
| aspsirna0938 | AUGACGACGCUGGUAUAGG UACUGCUGCGACCAUAUCC |
73 | 35 | 38 | AR | Spinal and Bulbar Muscular Atrophy, X-linked 1; SMAX1/Kennedy’s disease | c.172_174CAG(10_36) (p.Gln69_Gln80del)] | rs19392293 |
|
