Total number of Results for C1U are 15
Search:
ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna1982 UUUAUGAGGAUCUCUCUGG
AAAUACUCCUAGAGAGACC
85 30 55 P. luciferase NA NA NA
US2005/0176045A1
aspsirna1948 AAAGGGUGAGCGUGGUCCG
UUUCCCACUCGCACCAGGC
NA NA 75 COL6A3 Dominant ullrich muscular dystrophy (IVS16DS plus 1G-A) in intron 16 NA
24518369
aspsirna1952 GGCCAAAGGGUGAGCGUGG
CCGGUUUCCCACUCGCACC
NA NA 60 COL6A3 Dominant ullrich muscular dystrophy (IVS16DS plus 1G-A) in intron 16 NA
24518369
aspsirna1955 UCGGGCCAAAGGGUGAGCG
AGCCCGGUUUCCCACUCGC
NA NA 5 COL6A3 Dominant ullrich muscular dystrophy (IVS16DS plus 1G-A) in intron 16 NA
24518369
aspsirna1957 GUAGCCCGGUUUCCCACUG
CAUCGGGCCAAAGGGUGAC
NA NA 40 COL6A3 Dominant ullrich muscular dystrophy (IVS16DS plus 1G-A) in intron 16 NA
24518369
aspsirna1959 AAAGGGUGAGCGUGGUCCG
UUUCCCACUCGCACCAGGC
NA NA 78 COL6A3 Dominant ullrich muscular dystrophy (IVS16DS plus 1G-A) in intron 16 NA
24518369
aspsirna1963 GGCCAAAGGGUGAGCGUGG
CCGGUUUCCCACUCGCACC
NA NA 67 COL6A3 Dominant ullrich muscular dystrophy (IVS16DS plus 1G-A) in intron 16 NA
24518369
aspsirna1966 UCGGGCCAAAGGGUGAGCG
AGCCCGGUUUCCCACUCGC
NA NA 8 COL6A3 Dominant ullrich muscular dystrophy (IVS16DS plus 1G-A) in intron 16 NA
24518369
aspsirna1968 GUAGCCCGGUUUCCCACUG
CAUCGGGCCAAAGGGUGAC
NA NA 58 COL6A3 Dominant ullrich muscular dystrophy (IVS16DS plus 1G-A) in intron 16 NA
24518369
aspsirna1970 AAAGGGUGAGCGUGGUCCA
UUUCCCACUCGCACCAGGC
60 40 20 COL6A3 Congenital muscular dystrophy type Ullrich (UCMD) (IVS16DS plus 1G-A) in intron 16 NA
24518369
aspsirna1974 GGCCAAAGGGUGAGCGUGA
CCGGUUUCCCACUCGCACC
70 25 45 COL6A3 Congenital muscular dystrophy type Ullrich (UCMD) (IVS16DS plus 1G-A) in intron 16 NA
24518369
aspsirna1977 UCGGGCCAAAGGGUGAGCA
AGCCCGGUUUCCCACUCGC
76 50 26 COL6A3 Congenital muscular dystrophy type Ullrich (UCMD) (IVS16DS plus 1G-A) in intron 16 NA
24518369
aspsirna1979 CAUCGGGCCAAAGGGUGAA
GUAGCCCGGUUUCCCACUC
86 60 26 COL6A3 Congenital muscular dystrophy type Ullrich (UCMD) (IVS16DS plus 1G-A) in intron 16 NA
24518369
aspsirna3579 UCAGAGAGAUCCUCAUAAA
AGUCUCUCUAGGAGUAUUC
90 45 45 PPIB/Cyclophilin B PPIB-Related Osteogenesis Imperfecta (Type IX) NA NA
16489337
aspsirna3655 GGUUGGAGGAGAGAUGAUA
CCAACCUCCUCUCUACUAC
90 92 -2 PPIB/Cyclophilin B PPIB-Related Osteogenesis Imperfecta (Type IX) NA NA
16489337
Showing 1 to 15 of 15 entries