ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna1982 | UUUAUGAGGAUCUCUCUGG AAAUACUCCUAGAGAGACC |
85 | 30 | 55 | P. luciferase | NA | NA | NA | ![]() |
|
aspsirna1948 | AAAGGGUGAGCGUGGUCCG UUUCCCACUCGCACCAGGC |
NA | NA | 75 | COL6A3 | Dominant ullrich muscular dystrophy | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1952 | GGCCAAAGGGUGAGCGUGG CCGGUUUCCCACUCGCACC |
NA | NA | 60 | COL6A3 | Dominant ullrich muscular dystrophy | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1955 | UCGGGCCAAAGGGUGAGCG AGCCCGGUUUCCCACUCGC |
NA | NA | 5 | COL6A3 | Dominant ullrich muscular dystrophy | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1957 | GUAGCCCGGUUUCCCACUG CAUCGGGCCAAAGGGUGAC |
NA | NA | 40 | COL6A3 | Dominant ullrich muscular dystrophy | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1959 | AAAGGGUGAGCGUGGUCCG UUUCCCACUCGCACCAGGC |
NA | NA | 78 | COL6A3 | Dominant ullrich muscular dystrophy | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1963 | GGCCAAAGGGUGAGCGUGG CCGGUUUCCCACUCGCACC |
NA | NA | 67 | COL6A3 | Dominant ullrich muscular dystrophy | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1966 | UCGGGCCAAAGGGUGAGCG AGCCCGGUUUCCCACUCGC |
NA | NA | 8 | COL6A3 | Dominant ullrich muscular dystrophy | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1968 | GUAGCCCGGUUUCCCACUG CAUCGGGCCAAAGGGUGAC |
NA | NA | 58 | COL6A3 | Dominant ullrich muscular dystrophy | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1970 | AAAGGGUGAGCGUGGUCCA UUUCCCACUCGCACCAGGC |
60 | 40 | 20 | COL6A3 | Congenital muscular dystrophy type Ullrich (UCMD) | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1974 | GGCCAAAGGGUGAGCGUGA CCGGUUUCCCACUCGCACC |
70 | 25 | 45 | COL6A3 | Congenital muscular dystrophy type Ullrich (UCMD) | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1977 | UCGGGCCAAAGGGUGAGCA AGCCCGGUUUCCCACUCGC |
76 | 50 | 26 | COL6A3 | Congenital muscular dystrophy type Ullrich (UCMD) | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1979 | CAUCGGGCCAAAGGGUGAA GUAGCCCGGUUUCCCACUC |
86 | 60 | 26 | COL6A3 | Congenital muscular dystrophy type Ullrich (UCMD) | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna3579 | UCAGAGAGAUCCUCAUAAA AGUCUCUCUAGGAGUAUUC |
90 | 45 | 45 | PPIB/Cyclophilin B | PPIB-Related Osteogenesis Imperfecta (Type IX) | NA | NA | ![]() |
|
aspsirna3655 | GGUUGGAGGAGAGAUGAUA CCAACCUCCUCUCUACUAC |
90 | 92 | -2 | PPIB/Cyclophilin B | PPIB-Related Osteogenesis Imperfecta (Type IX) | NA | NA | ![]() |