| ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
|---|---|---|---|---|---|---|---|---|---|---|
| aspsirna2042 | CUCUCCUGUAGCUAAGGGC GAGAGGACAUCGAUUCCCG |
83 | 45 | 38 | PPIB/Cyclophilin B | NA | NA | NA | 
|
|
| aspsirna0467 | UUCCUGGAGCAGCAGAAGA AAGGACCUCGUCGUCUUCU |
40 | 0 | 40 | KRT5 | Epidermolysis bullosa simplex (EBS) | c.579C>G, p.Asn193Lys | rs60586163 |
|
|
| aspsirna0505 | UUCCUGGAGCAGCAGAAGA AAGGACCUCGUCGUCUUCU |
40 | 0 | 40 | KRT5 | Epidermolysis bullosa simplex (EBS) | c.579C>G, p.Asn193Lys | rs60586163 |
|
|
| aspsirna0445 | UCAUUUUCUACAGUGUUGU AGUAAAAGAUGUCACAACA |
80 | 22 | 58 | PSEN1 | Alzheimers disease | c.811C>G, p.Leu271Val | rs63750886 |
|
|
| aspsirna0946 | GGAUGAGGAACAGCAACGU CCUACUCCUUGUCGUUGCA |
9 | 7 | 2 | AR | Spinal and Bulbar Muscular Atrophy, X-linked 1; SMAX1/Kennedy’s disease | c.172_174CAG(10_36) (p.Gln69_Gln80del)] | rs19392293 |
|
