Total number of Results for C3G are 5
ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
ASPsiRNA ID Mutant allele/ASP-siRNA Efficacy
for mutant(%)
Efficacy
for wild (%)
Relative Difference (%) Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna0113 CGAGUAAGCUAAAAACGAA
GCUCAUUCGAUUUUUGCUU
0 99 -99 PRNP Prion disease/Gerstmann-Straussler disease c.314C>T,p.Pro105Leu rs11538758
18493311
aspsirna0152 CGAGUAAGCUAAAAACGAA
GCUCAUUCGAUUUUUGCUU
0 99 -99 PRNP Prion disease/Gerstmann-Straussler disease c.314C>T,p.Pro105Leu rs11538758
18493311
aspsirna0444 CAUUUUCUACAGUGUUGUG
GUAAAAGAUGUCACAACAC
82 0 82 PSEN1 Alzheimers disease c.811C>G, p.Leu271Val rs63750886
21559198
aspsirna0468 UCCUGGAGCAGCAGAAGAA
AGGACCUCGUCGUCUUCUU
40 0 40 KRT5 Epidermolysis bullosa simplex (EBS) c.579C>G, p.Asn193Lys rs60586163
21716320
aspsirna0506 UCCUGGAGCAGCAGAAGAA
AGGACCUCGUCGUCUUCUU
40 0 40 KRT5 Epidermolysis bullosa simplex (EBS) c.579C>G, p.Asn193Lys rs60586163
21716320