ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna0384 | AGAUUUGGACCUGGGAGUC UCUAAACCUGGACCCUCAG |
35 | 65 | -30 | ACVR1 | Fibrodysplasia Ossificans Progressiva (FOP) | c.1067G>A,p.Gly356Asp | rs12191267 | ![]() |