Total number of Results for C5G,U11C are 1
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ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna0384 AGAUUUGGACCUGGGAGUC
UCUAAACCUGGACCCUCAG
35 65 -30 ACVR1 Fibrodysplasia Ossificans Progressiva (FOP) c.1067G>A,p.Gly356Asp rs12191267
22130450
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