ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna2054 | CUCUCCUGUAGCUGAGGCC GAGAGGACAUCGACUCCGG |
45 | 45 | 0 | PPIB/Cyclophilin B | NA | NA | NA | ![]() |
|
aspsirna2422 | AACUCCUCCGCGCGACUUU UUGAGGAGGCGCGCUGAAA |
55 | 70 | -15 | KRAS | NA | NA | NA | ![]() |
|
aspsirna0619 | UGAGAAGAGCACCGUGCAG ACUCUUCUCGUGGCACGUC |
90 | 49 | 41 | KRT9 | Epidermolytic palmoplantar keratoderma (EPPK) | c.469A>G ,p.Met157Val | rs58597584 | ![]() |
|
aspsirna3675 | GGUUGGAGGAGAGAUGAUA CCAACCUCCUCUCCACUAU |
90 | 79 | 11 | PPIB/Cyclophilin B | PPIB-Related Osteogenesis Imperfecta (Type IX) | NA | NA | ![]() |