ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna1999 | UUUAUGAGGAUCGCUCUGA AAAUACUCCUAGCGAGACU |
75 | 30 | 45 | P. luciferase | NA | NA | NA | ![]() |
|
aspsirna2056 | CUCUCCUGUAGCGAAGGCC GAGAGGACAUCGCUUCCGG |
5 | 45 | -40 | PPIB/Cyclophilin B | NA | NA | NA | ![]() |
|
aspsirna3602 | UCAGAGAGAUCCUCAUAAA AGUCUCUCUAGGCGUAUUU |
90 | 75 | 15 | PPIB/Cyclophilin B | PPIB-Related Osteogenesis Imperfecta (Type IX) | NA | NA | ![]() |
|
aspsirna1834 | AAGCAGCACAAUGAGGAGUGC UUCGUCGUGUUACUCCUCACG |
NA | 72 | NA | Fen1 | Werner syndrome | NA | NA | ![]() |