ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna0620 | GAGAAGAGCACCGUGCAGG CUCUUCUCGUGGCACGUCC |
100 | 50 | 50 | KRT9 | Epidermolytic palmoplantar keratoderma (EPPK) | c.469A>G ,p.Met157Val | rs58597584 | ![]() |
|
aspsirna3756 | AAAGUUGCGCGGAGGAGUU UUUCAACGCGCCCCCUCAA |
90 | 54 | 36 | PPIB/Cyclophilin B | PPIB-Related Osteogenesis Imperfecta (Type IX) | NA | NA | ![]() |